Two of Opus's seven gene therapy assets are in clinical trials, with additional programs expected to enter the clinic.

Scientists from UC Davis Center for Surgical Bioengineering, the MIND Institute and UC Berkeley’s Murthy Lab are developing ...

This penguin’s features are very special and rare. @bbcearth explains, "This Gentoo penguin's stark white [color] is the ...

A rare form of diabetes affecting newborn babies and caused by a genetic disorder has been discovered by scientists in the UK ...

Tigers are some of the most evasive creatures on the planet. They stalk through forests, savannahs, grasslands, and ...

A new study by UCLA scientists adds to the understanding of the genetic architecture of schizophrenia. Past research has shown the impact of commonly occurring genetic variants on a person's risk of ...

A long-established drug with a diverse medical history is drawing new attention for its potential role in treating an ultra-rare and life-threatening genetic disorder. Early findings suggest that a me ...

A Northwestern Medicine study has uncovered a promising new therapeutic approach for a rare genetic brain disorder, according ...

Kaitlyn and Gerard Norton welcomed their daughter, Madeline, into the world. Six months later, the family found itself in a unique situation, regularly traveling to another state for medical care and ...