As CRISPR moves from lab success to real-world medicine, 2026 will test whether these revolutionary gene-editing therapies can reach the patients who need them most or remain costly, complex ...

Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...

Scientists have discovered a new CRISPR mechanism with precise activity, expanding the potential applications of the existing ...

Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...

Innovative research into the gene-editing tool targets influenza’s ability to replicate—stopping it in its tracks.

The CRISPR gene-editing tool can be used to silence an important hepatitis B virus gene, a proof-of-concept in vitro study suggests. "It's the first time we've seen CRISPR editing done in a hepatitis ...

An infant with a rare metabolic disease became the world’s first patient to be treated with a personalized CRISPR gene-editing treatment in a landmark study between Penn Medicine and the Children’s ...

The CRISPR gene editing technology has transformed the research lab, and this powerful tool is now making its way into the clinic. So far, three different human diseases have been successfully treated ...

The study used large-scale CRISPR gene-editing technology to systematically determine which genes are required as embryonic ...

A large genetic screen has revealed how stem cells transform into brain cells, exposing hundreds of genes that make this ...

By editing thousands of genes in mouse stem cells, the scientists identified a list of over 300 that are crucial for neural differentiation.

Three factors will shape development of gene- and other edited therapies over the coming year and beyond. First, commercially speaking, edited therapies still see lower than expected uptake among ...